I am a paediatric research nurse and I have worked on the CRF since 2012 delivering early phase clinical trials to both children and adults. The disease areas I have worked with on clinical trials have included DMD, SMA, Achondroplasia, Haemophilia and JIA. Other clinical trials in set up are looking at epilepsy, mitochondrial disease and autism treatments. We enrol participants regionally, nationally and internationally.
We have a dedicated paediatric area within the department and aim to deliver family centred, holistic care working with both academic and pharmaceutical partners to develop new treatments for chronic and rare diseases. We have delivered the first UK Pfizer DMD gene therapy dose in May 2021 and I am currently involved in the set-up of a number of other gene therapy studies.
I worked on a busy general paediatric ward for 8 years prior to coming into research, which has given me a good knowledge of numerous disease areas.